Amicus Therapeutics

🎙️New DNA Today podcast episode out now, sponsored by Amicus, features Dr. Amy Kritzer discussing Fabry disease. She explores differences of the disease by sex, challenges to early detection, cascade screening and the psychosocial impact of a diagnosis.   🎧Give it a listen at  DNAToday.com or wherever you get your podcasts. https://lnkd.in/eeFP434y   *Intended for U.S. healthcare professionals

Amicus was honored to sponsor the BioNJ Annual Meeting and Innovation Celebration last evening and to recognize the strength and spirit of New Jersey’s biotech and pharmaceutical community. We’re deeply grateful to the patients and patient advocates who shared their stories and experiences. Their voices remind us why this work matters and highlight the outsized impact New Jersey's biotech and pharmaceutical innovation continues to have here at home and around  the world.   Thank you to our newly retired Chief Patient Advocate, Jayne Gershkowitz, for her dedicated service on the BioNJ board, and congratulations to Chief Corporate Affairs Officer, Mary Elizabeth Blake, on being named to the BioNJ board. #BioNJ #PatientsCantWait

The Exhibit Hall at #WORLDSymposium2026 in San Diego opens today at 3:30 pm PST. Stop by booth #101 to connect with our team and learn about our mission to develop and deliver transformative medicines for people living with rare diseases.

We’re presenting new long-term data from clinical and real-world studies in Fabry disease and in Pompe disease at this year’s WORLDSymposium. Learn more here: https://lnkd.in/e2Gmkgic

We’re proud to sponsor several sessions this week at #WORLDSymposium2026. For more information on these sessions, check out the full presentations program here: https://lnkd.in/d_YTnED

We’re heading to San Diego for #WORLDSymposium2026! This global meeting is an important opportunity to advance research and innovation for people living with lysosomal diseases. Every breakthrough starts with a shared commitment to improving lives, and we’re proud to join the community of scientists, clinicians, and advocates working toward better treatments and brighter futures for people living with rare diseases and their families.

“After searching for five years looking for a diagnosis, I heard the word Fabry for the first time.”   Darrick’s journey to a Fabry disease diagnosis is far from unique. With symptoms that often mimic other conditions, Fabry can go undetected for years, delaying treatment and impacting lives.   To help healthcare professionals (HCPs) recognize the signs earlier, we launched FindingFabry.com: a new resource to help HCPs spot the signs of #FabryDisease earlier, navigate diagnostic steps, and connect patients with the treatment they need.   Explore the site and help bring this hidden disease into focus. https://findingfabry.com/   NP-NN-US-00021025

Dr. Martin Luther King, Jr. asked a question that still calls us to act: “What are you doing for others?” For Amicus, the answer is woven into our mission—to develop and deliver transformative medicines for people living with rare diseases—and into how we show up in our communities. From organized days of service to everyday acts of care, our team turns compassion into meaningful impact. This #MLKDay, we recommit to service—today, tomorrow, and all year long.

As we welcome 2026, we hope this year brings you hope, health, and joy. We remain committed to advancing science, delivering transformative medicines, and supporting the rare disease community every step of the way. Cheers to a year of progress and possibilities!

From all of us at Amicus, we wish you and your loved ones a joyful holiday season!