🔍 Sharing this insightful video from our collaborators at AviadoBio, highlighting the neurosurgical techniques supporting this exciting clinical trial in gene therapy. The precision involved in delivering these therapies is remarkable — and directly influences patient outcomes. We're proud to be delivering therapies that are helping to expand treatment possibilities in this space.

Today, Jaguar Gene Therapy released an updated JAG201 clinical trial community letter and FAQ. The document, with new information highlighted in blue, is available here: https://lnkd.in/eFQB82ez. #phelanmcdermidsyndrome #shank3 #genetherapy #clinicaltrials 

"The value proposition (of #CellandGeneTherapy) cannot be only based on the fantastic science and clinical efficacy. It needs to be anchored in the business case for patient access." Insight and perspective from the President's Desk courtesy of ISCT, International Society for Cell & Gene Therapy - and Miguel Forte of course! #CellTherapy #GeneTherapy #Autologous #Allogeneic #ExVivo #InVivo https://lnkd.in/gEbB-qqR

For the first time, doctors have successfully slowed progression of Huntington’s by 75% using a one-time gene therapy delivered directly into the brain. This landmark trial builds on years of research in rodents, minipigs, and monkeys, where the therapy was tested for efficacy and safety before reaching patients. 👉Read the full article here: https://lnkd.in/e3hxzzi4 🔗For more information about the animal studies that made this work possible, visit: https://lnkd.in/e3zPzqih

How can cell & gene therapy rebound from manufacturing challenges and shifting investor confidence? Check out Part 1 of our interview with Alliance for Regenerative Medicine's Miguel Forte during #CGMesa25 at https://hubs.ly/Q03NQ5j_0 #meetingonthemesa #CellTherapy #GeneTherapy #BiotechInnovation #CGT #HealthcareTrends

Cures of Duchenne (Detailed List of All Clinical Trials) List of all researches such as gene therapy, exon skipping, reducing inflammation and improving muscle growth & protection cures for duchenne muscular dystrophy. https://lnkd.in/dqQu8zgZ

Every step in gene therapy manufacturing matters, but cell lysis plays a critical role in ensuring process efficiency and product consistency. In a recent Q&A with The Medicine Maker, Beth Fahnestock, Director of New Product Innovations at Avantor®, shares how optimizing cell lysis can drive more effective viral vector production, support scalability from research to commercial manufacturing and improve overall process sustainability. Read the full article: https://ow.ly/Oygj50Xcp7M #GeneTherapy #Bioprocessing #CellLysis #ViralVectors

I've recently been learning about cell and gene therapy for a story about Oxford Biomedica. Its shares rallied 76% this quarter, helped by a growing US manufacturing presence that has kept it away from the glare of President Donald Trump’s tariffs regime. Oxford Biomedica produces viral vectors, which are key components of cell and gene therapy because they’re designed to deliver genetic material to the cells of patients. The stock was the second-best performer in the UK's midcap index this quarter. You can read my story here: https://lnkd.in/epuVHaBr #markets #stocks #uk #cdmo #cgt #viralvectors #ftse250

The Federal Circuit will hear arguments in cases where a nearly $42 million patent win for Seagen hangs in the balance and where Regenxbio is seeking to undo the invalidation of its gene therapy patent for covering a natural product. https://lnkd.in/eNRrEssi

Hemophilia stands out among rare diseases for its remarkable therapeutic progress, a success built on decades of innovation, scientific discovery, and investment. From the cloning of FVIII and FIX genes to the arrival of gene therapy, each milestone has transformed lives. Global advocacy by WFH, EAHAD, and NBDF has been key to ensuring access and safety. Yet, sustaining this progress requires continued commitment and investment, so that every person with hemophilia can benefit from the full promise of science. #Hemophilia #Innovation #GeneTherapy #Haematology